Riluzole, a drug approved to treat amyotrophic lateral sclerosis (ALS), a disease affecting nerve cells controlling movement, could slow the gradual loss of a particular brain cell that occurs in Niemann-Pick disease type C1 (NPC1), a rare genetic disorder affecting children and adolescents, suggests a study in mice.
Repurposed ALS drug shows promise in mouse model of rare childhood genetic disorder
- ScienceDaily
- 19. 11 2021 (21:55)